Latest papers

Self-complementary AAV-mediated gene therapy restores cone function and prevents cone degeneration in two models of Rpe65 deficiency.

Combined paracrine and endocrine AAV9 mediated expression of hepatocyte growth factor for the treatment of renal fibrosis.

Retinoid x receptor gamma control of affective behaviors involves dopaminergic signaling in mice.

Distinct roles of synaptic transmission in direct and indirect striatal pathways to reward and aversive behavior.

Chromosomal position effects on AAV-mediated gene targeting.

Efficacy of recombinant adeno-associated viral vectors serotypes 1, 2, and 5 for the transduction of pancreatic and colon carcinoma cells.

A viral assembly factor promotes AAV2 capsid formation in the nucleolus.

Regulation of retinal function but nonrescue of vision in RPE65-deficient dogs treated with doxycycline-regulatable AAV vectors.

Adeno-associated virus harboring fusion gene NT4-ant-shepherdin induce cell death in human lung cancer cells.

Delivering the goods: viral and non-viral gene therapy systems and the inherent limits on cargo DNA and internal sequences.

Reengineered AAV vectors: old dog, new tricks.

[Construction and identification of recombinant adeno-associated virus expressing siRNA].

Changes in adeno-associated virus-mediated gene delivery in retinal degeneration.

Treatment of hepatocellular carcinoma with adeno-associated virus encoding interleukin-15 superagonist.

Fate of recombinant adeno-associated viral vector genomes during DNA double-strand break-induced gene targeting in human cells.

rAAV9--a human-derived adeno-associated virus vector for efficient transgene expression in mouse cingulate cortex.

BALB/c mice show impaired hepatic tolerogenic response following AAV gene transfer to the liver.

Comparison of AAV serotypes for gene delivery to dorsal root ganglion neurons.

AAV provides an alternative for gene therapy of the peripheral sensory nervous system.

Comparison of adeno-associated virus pseudotype 1, 2, and 8 vectors administered by intramuscular injection in the treatment of murine phenylketonuria.